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Category: clinical trial

Best Disease Gene Therapy Advances Toward Clinical Trial

Source: Foundation Fighting Blindness Blog – Eye on the Cure – Best Disease Gene Therapy Advances Toward Clinical Trial Audio version: Untreated retina Retina treated with gene therapy Using gene therapy, FFB-funded researchers at the University of Pennsylvania School of Veterinary Medicine (Penn Vet) and Perelman School of Medicine…

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ProQR Doses First Participant in Its LCA10 Therapy Clinical Trial

Source: Foundation Fighting Blindness Blog – Eye on the Cure – ProQR Doses First Participant in Its LCA10 Therapy Clinical Trial ProQR, a biotech company in the Netherlands, has treated its first patient in a Phase 1/2 clinical trial for QR-110, a therapy for people with Leber congenital amaurosis…

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FDA Committee Unanimously Recommends Approval for Spark’s RPE65 Gene Therapy – Final Decision Due in January 2018

Source: Foundation Fighting Blindness Blog – Eye on the Cure – FDA Committee Unanimously Recommends Approval for Spark’s RPE65 Gene Therapy – Final Decision Due in January 2018 Ashley and Cole Carper traveled from Little Rock, AR, to tell their family’s story at the FDA hearing. Spark Therapeutics has…

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MeiraGTx Treats First Patient in XLRP Gene-Therapy Trial

Source: Foundation Fighting Blindness Blog – Eye on the Cure – MeiraGTx Treats First Patient in XLRP Gene-Therapy Trial MeiraGTx, a gene-therapy company in London and New York City, has treated its first patient in a gene-therapy clinical trial for people with X-linked retinitis pigmentosa (XLRP) caused by mutations…

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Twelve People Receive XLRS Gene Therapy in AGTC’s Clinical Trial

Source: Foundation Fighting Blindness Blog – Eye on the Cure – Twelve People Receive XLRS Gene Therapy in AGTC’s Clinical Trial Applied Genetics Technology Corporation (AGTC) reported that its gene therapy for X-linked retinoschisis (XLRS) has performed encouragingly in a Phase I/II, safety-oriented clinical trial taking place at seven…

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